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Gene therapy for spinal muscular atrophy: timing is key.

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  • Additional Information
    • Publication Information:
      Elsevier Ltd, 2024.
    • Publication Date:
      2024
    • Relation:
      https://api.elsevier.com/content/article/PII:S2666776224002795?httpAccept=text/xml; urn:issn:2666-7762
    • Accession Number:
      10.1016/j.lanepe.2024.101112
    • Rights:
      open access
      http://purl.org/coar/access_right/c_abf2
      info:eu-repo/semantics/openAccess
    • Accession Number:
      edsorb.324864