Item request has been placed! ×
Item request cannot be made. ×
loading  Processing Request
Item request has been placed! ×
Item request cannot be made. ×
loading  Processing Request

Wilson's disease in Spain: validation of sources of information used by the Rare Diseases Registries

Subjects: Adult; Male; medicine.medical_specialty

  • Source: RepisaludInstituto de Salud Carlos III (ISCIII)Academica-e. Repositorio Institucional de la Universidad Pública de NavarrainstnameGaceta Sanitaria, Vol 35, Iss 6, Pp 551-558

Record details

×

Outcomes of progranulin gene therapy in the retina are dependent on time and route of delivery

Subjects: Retinal degeneration; Aging; retina

  • Source: Molecular Therapy. Methods & Clinical DevelopmentMolecular Therapy: Methods & Clinical Development, Vol 22, Iss, Pp 40-51 (2021)

Record details

×
  • 1-10 of  385 results for ""Rare Diseases""